Today's Rundown Featured Story | | | Wednesday, September 5, 2018 Sangamo’s big chance has come to show it has a safe and efficient gene-editing technique to rival CRISPR—and the initial response has been a little mixed. |
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| This week's sponsor is Trianni. | |  | |
Top Stories Wednesday, September 5, 2018 It has not been a great 12 months for Vivek Ramaswamy’s constellation of biotechs—seeing a major meltdown at Axovant with failures and a fleeing CEO—and now it’s losing another star biotech player in Jackie Fouse, Ph.D. Wednesday, September 5, 2018 Sean Harper, M.D., has revealed his next move. The former head of R&D at Amgen is teaming up with Beth Seidenberg, M.D., to lead investing activities at Westlake Village BioPartners, a new West Coast venture capital shop that has $320 million to pump into biotechs. Wednesday, September 5, 2018 Teva has finally given up on laquinimod. The aryl hydrocarbon receptor activator was once hailed as a blockbuster heir to Copaxone but suffered a string of late-phase failures that dragged down Teva and its partner Active Biotech. Wednesday, September 5, 2018 ProQR Therapeutics reported interim phase 1/2 data for its RNA-based treatment for LCA10, a severe form of blindness caused by a rare genetic disorder. The majority of patients had a “clinically meaningful” improvement in vision after three months of treatment, and the Dutch biotech is planning a pivotal trial for 2019. Tuesday, September 4, 2018 Endocrine therapy developer Radius Health has brought on Charles Morris to be its new chief medical officer and oversee the company’s expansion into oncology, with two breast cancer treatments currently in early-phase clinical trials. Wednesday, September 5, 2018 Fierce 15 winner Fulcrum Therapeutics has pulled in an impressive $80 million series B financing deal as it looks to push on with its lead drug into clinical testing. Wednesday, September 5, 2018 PhaseBio raised $34 million in its series D round, which will advance its lead assets: a treatment for pulmonary arterial hypertension (PAH) developed in-house and a reversal agent of AstraZeneca’s clot-busting Brilinta, licensed from the British pharma in 2017. Wednesday, September 5, 2018 Biohaven Pharmaceutical has licensed an experimental treatment of the neurodegenerative disorder multiple system atrophy from AstraZeneca. The deal follows a midphase trial that linked oral myeloperoxidase inhibitor AZD3241 to numerical improvements on a scale of MSA symptoms. Wednesday, September 5, 2018 Gossamer Bio has tapped Bristol-Myers Squibb’s immunology and cancer R&D executive Luisa Salter-Cid, Ph.D., as its new research lead. Resources Sponsored by: Patheon, part of Thermo Fisher Scientific When developing a parenteral, pharmaceutical scientists are faced with a variety of choices – choices that can be conflicting or present differing advantages. Sponsored by: Baxter Baxter BioPharma Solutions’ whitepaper offers a method to address the challenges of tech transfer for lyophilized products from lab-scale to commercial-scale. Sponsored by: Blue Matter A whitepaper outlining the key commercial challenges facing rare disease products, and how biopharmaceutical companies can overcome them. Sponsored by: AWS and Tableau Inova is using the capabilities of Tableau on AWS to identify biomarkers for personalized treatment intended to improve health outcomes for children. Sponsored by: Catalent In this case study, an unknown leachable species was detected by GC-MS analysis of an alkaline drug product (pH approximately 10.5) that was packaged in a novel self- contained plastic Blow Fill Seal (BFS) vial. Sponsored by: AWS and Reltio Reltio and IQVIA provide holistic data management solutions for traditional pharma, emerging biotech, and consumer health companies, on AWS. Presented by: AWS and Druva Life Sciences organizations are embracing cloud-based Master Data Management (MDM) to modernize the organization of critical data. Sponsored by: Catalent Catalent provides world class stability services to ease your critical path to success. Sponsored by: Health Strategies Group The window of market exclusivity continues to narrow dramatically in the global marketplace. Given this demanding environment, your global market access team faces increasing urgency to get the value proposition right at the time of launch. Sponsored by: Biotech Primer The Biopharma industry is moving at lightning speed and it can be a challenge to keep pace. Here at Biotech Primer we spend hours each week researching, writing, and editing original content for the Biotech Primer WEEKLY with one goal in mind: to help everyone better understand the latest science and technology driving today’s healthcare industry. Sponsored by: PharmaCord When was the last time your patient support program perfectly aligned with the patient journey, solving all the critical gaps in positioning your brand for success? Follow the 3-D approach to your solution design, and you will achieve a better outcome for your patients. Sponsored by: Catalent Develop a basic understanding of principles and concepts of bioavailability of oral drugs. Drug Approval, Manufacturing Quality & Regulation 2018 | Online RESI HealthTech Week September 5-7, 2018 | Boston, MA 2018 Latin America Healthcare Compliance Certification Program September 24-27, 2018 | Sao Paulo, Brazil Drug Development Immersion September 26-27, 2018 | West Windsor, NJ FierceBiotech 3rd Drug Development Forum October 1–3, 2018 | Hilton Boston Logan Airport Hotel | Boston, MA Compliance Certification Program at Seton Hall Law October 8-11, 2018 | Newark, NJ BioImmersion: Biotech for the Non-Scientist October 16-18, 2018 | Chicago, IL Fierce Innovation Awards: Life Sciences Edition 2018 FierceBiotech Executive Summit: London October 30, 2018 | Royal Society of Medicine Understanding Commercialization Within Biopharma Nov 7-8, 2018 | Boston, MA Drug Development Boot Camp® 2018 – Register Now! November 14-15, 2018 | Boston, MA | Register now and start your pre-Boot Camp preparation Drug Development Immersion December 5-6, 2018 | San Diego, CA Understanding Drug Pricing and Reimbursement December 12, 2018 | Boston, MA | 
