| Gene therapy, medical science's next frontier, holds great promise for treating conditions from cancer and hemophilia to Huntington's disease and cystic fibrosis.
In a new white paper, Premier Research explores the past, present, and future of gene therapy trials. Topics include: - The three main gene therapy vectors and delivery systems: viral vectors, non-viral vectors, and engineered nucleases
- Operational considerations such as vendor and site selection, explaining these incredibly complex studies to patients and families, and creating backup and risk mitigation plans
- Identifying patients — especially difficult when working in rare genetic conditions — and retaining them through long follow-up periods
Understanding these challenges is vital to realizing gene therapy's vast potential.
Read our white paper for important insights into achieving operational excellence in these trials. Premier Research. It's what we do. Best. |
